Science:
Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
The STOP ALD Foundation:
Gene Therapy Success in Severe Brain Disorder Applauded by The Stop ALD Foundation
Affected Families Achieve Goal of Saving Children Exciting Results Reported in Science
AAAS:
Science: Gene Therapy Technique Slows “Lorenzo’s Oil” Brain Disease
NATURE:
Brain disease treated by gene therapy
SCIENCE:
Gene Therapy Halts Brain Disease in Two Boys
The New York Times:
After Setbacks, Small Successes for Gene Therapy
ABC News:
Scientists Halt Brain Disease With New Gene Therapy
NPR:
Rare Disease Treated Using Gene Therapy
The Philadelphia Inquirer:
Sisters rally genetic researchers to tackle fatal brain disease
Bloomberg:
Gene Therapy Saves Two Boys From Rare Brain Disease
Elmundo.Es:
El 'milagro' de Andy y Ángel
AJC:
Gene Therapy for Fatal Brain Disorder 'Just the Beginning'
Estadao.com.br
Terapia gênica barra doença degenerativa
Los Angeles Times:
Gene therapy makes major stride in 'Lorenzo's Oil' disease
WIRED:
Gene Therapy Halts Fatal Brain Disease
AP:
New gene therapy halts 2 boys' rare brain disease
The Canadian Press:
French scientists appear to halt rare brain disease in 2 boys with new gene therapy approach
Forbes:
New gene therapy halts 2 boys' rare brain disease
CBC News
Gene therapy halts rare brain disease
The Independant:
Gene therapy beats back brain wasting disease
St. Petersburg Times:
These three moms are on a mission to beat the genetic disease ALD
Times Online:
Gene therapy could cure Lorenzo’s Oil brain disease